CNP analogue
Vosoritide clinical trials
Answer
Vosoritide has 23 registered trials: 12 running, 4 completed, 0 stopped early. 3 posted results.
Trial registerClinicalTrials.gov and EU CTIS, read 2026-10-03
| Trial | Title | Status | Phase | Registered | Results |
|---|---|---|---|---|---|
| NCT07441876 Trial register | Study to Evaluate the Efficacy and Safety of BMN 333 Versus Vosoritide in Children With Achondroplasia | currently recruiting participants | - | 2026-03-02 | - |
| NCT06668805 Trial register | A Study of Vosoritide in Children With Noonan Syndrome With Inadequate Growth During or After Human Growth Hormone Treatment | running, but no longer enrolling | - | 2024-10-31 | - |
| 2024-512261-14-00 Trial register | A Phase 2, Randomized, Double-Blind, Placebo-Controlled, Multicenter Study to Evaluate the Safety and Efficacy of Vosoritide in Infants and Young Children with | Not stated | 2 | - | - |
| NCT07073014 Trial register | Long-Term Extension Study of Vosoritide to Treat Children With Hypochondroplasia | enrolling by invitation only | - | 2025-07-18 | - |
| 2024-520137-74-00 Trial register | A Phase 2, Randomized, Controlled, Multicenter Study of Vosoritide in Children With Idiopathic Short Stature | Not stated | 2 | - | - |
| 2024-517238-16-00 Trial register | A Phase 3, Open-Label, Long-Term Extension Study to Evaluate the Safety and Efficacy of Vosoritide in Children with Hypochondroplasia | Not stated | 3 | - | - |
| 2024-515861-33-00 Trial register | A Phase 2, Randomized, Multicenter, Study of Vosoritide in Children with Noonan Syndrome with Inadequate Growth During or After Human Growth Hormone Treatment | Not stated | 2 | - | - |
| NCT06382155 Trial register | A Phase 2 Study of Vosoritide in Children With Idiopathic Short Stature | currently recruiting participants | - | 2024-04-24 | - |
| 2024-513129-22-00 Trial register | A Phase 3, Randomized, Double-Blind, Placebo-Controlled, Multicenter Study to Evaluate the Efficacy and Safety of Vosoritide in Children with Hypochondroplasia | Not stated | 3 | - | - |
| 2025-523811-12-00 Trial register | A Multicenter, Randomized, Operationally Seamless Phase 2/3 Study to Evaluate the Efficacy and Safety of BMN 333 versus Vosoritide in Children with Achondroplas | Not stated | 2/3 | - | - |
| NCT07126262 Trial register | A Study of Vosoritide Versus Placebo in Children With Hypochondroplasia Aged 0 to < 36 Months | currently recruiting participants | - | 2025-08-17 | - |
| NCT04219007 Trial register | Vosoritide for Selected Genetic Causes of Short Stature | running, but no longer enrolling | - | 2020-01-06 | - |
| NCT02724228 Trial register | A Study to Evaluate Long-Term Safety, Tolerability, & Efficacy of BMN 111 in Children With Achondroplasia (ACH) | running, but no longer enrolling | - | 2016-02-12 | - |
| NCT03424018 Trial register | An Extension Study to Evaluate the Efficacy and Safety of BMN 111 in Children With Achondroplasia | running, but no longer enrolling | - | 2017-12-28 | - |
| NCT03989947 Trial register | An Extension Study to Evaluate Safety and Efficacy of BMN 111 in Children With Achondroplasia | running, but no longer enrolling | - | 2019-05-22 | - |
| NCT04554940 Trial register | A Clinical Trial to Evaluate Safety of Vosoritide in At-risk Infants With Achondroplasia | running, but no longer enrolling | - | 2020-09-18 | - |
| NCT05845749 Trial register | Safety and Efficacy of Voxzogo for Growth Deficits in MPS IVA and VI | running, but no longer enrolling | - | 2023-05-06 | - |
| NCT06455059 Trial register | Interventional Study of Vosoritide for the Treatment of Children With Hypochondroplasia | running, but no longer enrolling | - | 2024-06-12 | - |
| NCT05849389 Trial register | Vosoritide for Short Stature in Turner Syndrome | last verified some time ago; the register no longer confirms its status | - | 2023-05-08 | - |
| NCT03583697 Trial register | A Clinical Trial to Evaluate the Safety and Efficacy of BMN 111 in Infants and Young Children With Achondroplasia | completed | - | 2018-06-14 | Posted |
| NCT03197766 Trial register | A Study to Evaluate the Efficacy and Safety of BMN 111 in Children With Achondroplasia | completed | - | 2017-05-23 | Posted |
| NCT02055157 Trial register | A Phase 2 Study of BMN 111 to Evaluate Safety, Tolerability, and Efficacy in Children With Achondroplasia | completed | - | 2013-04-18 | Posted |
| NCT01590446 Trial register | A Study to Evaluate Safety and Tolerability of BMN 111 Administered to Healthy Adult Volunteers | completed | - | 2012-03-14 | - |
Source: ClinicalTrials.gov and EU CTIS, read 2026-10-03. Not medical advice.
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